General Session: Gene Therapy and Gene Editing as a Treatment Option for Patients with Hemoglobinopathies (103)
Sickle cell disease is one of the most common inherited diseases in the Unites States, with a homozygous frequency of 1 in 400 African American births. The disease is associated with multiple complications including infections, veno-occlusive pain crisis, acute chest syndrome, and cerebrovascular accidents.
Haydar Frangoul, MD MS
Misty Evans, DNP APRN CPNP-AC BMTCN®
- CNE Hours